Condition: Charcot Marie Tooth Disease Intervention: Sponsors: Michael Shy; Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta; Johns Hopkins University; National Institute of Neurological Disorders and Stroke (NINDS); King's College Hospital NHS Trust; Nemours Children's Clinic; Stanford University; University of Pennsylvania; University of Rochester; Children's Hospital of Philadelphia; Sydney Children's Hospitals Network; Rare Diseases Clinical Research Network; Muscular Dystrophy Association; National Institutes of Health (NIH); Charcot-Marie-Tooth Association; Massachusetts General Hospital; Cedars-Sinai Medical Center; University of Miami; Dubowitz Neuromuscular Centre; University of Minnesota; University of Connecticut; University of Colorado, Denver; Detroit Medical Center; Ohio State University Recruiting
Conditions: Charcot-Marie-Tooth Disease, Type IA; Charcot-Marie-Tooth Disease Type 2A; Charcot-Marie-Tooth Disease, Type IB; Charcot-Marie-Tooth Disease, Type X Intervention: Sponsors: University College, London; University of Iowa Recruiting